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1. (WO2018085842) THERAPEUTIC TARGETS FOR FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

Pub. No.:    WO/2018/085842    International Application No.:    PCT/US2017/060410
Publication Date: Sat May 12 01:59:59 CEST 2018 International Filing Date: Wed Nov 08 00:59:59 CET 2017
IPC: G01N 33/68
G01N 33/50
C12N 5/077
Applicants: UNIVERSITY OF MASSACHUSETTS
Inventors: JONES, Peter, L.
GREEN, Michael, R.
Title: THERAPEUTIC TARGETS FOR FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
Abstract:
The disclosure relates to methods and compositions for regulating expression of DUX4. In some aspects, methods described by the disclosure are useful for treating a disease associated with aberrant DUX4 expression (e.g., facioscapulohumeral muscular dystrophy).