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1. (WO2018009838) COMPOSITIONS AND METHODS RELATED TO THERAPEUTIC CELL SYSTEMS EXPRESSING EXOGENOUS RNA
Latest bibliographic data on file with the International Bureau    Submit observation

Pub. No.: WO/2018/009838 International Application No.: PCT/US2017/041155
Publication Date: 11.01.2018 International Filing Date: 07.07.2017
IPC:
C12N 5/078 (2010.01)
Applicants: HARANDI, Omid[US/US]; US
KHANWALKAR, Urjeet[IN/US]; US
HARIHARAN, Sneha[IN/US]; US
RUBIUS THERAPEUTICS, INC.[US/US]; 620 Memorial Dr #100W Cambridge, MA 02139, US
Inventors: HARANDI, Omid; US
KHANWALKAR, Urjeet; US
HARIHARAN, Sneha; US
KAHVEJIAN, Avak; US
MATA-FINK, Jordi; US
DEANS, Robert, J.; US
Agent: ZHANG, Wei; US
KOYFMAN, Hannah, R.; US
Priority Data:
62/359,41607.07.2016US
Title (EN) COMPOSITIONS AND METHODS RELATED TO THERAPEUTIC CELL SYSTEMS EXPRESSING EXOGENOUS RNA
(FR) COMPOSITIONS ET PROCÉDÉS ASSOCIÉS À DES SYSTÈMES CELLULAIRES THÉRAPEUTIQUES EXPRIMANT DE L'ARN EXOGÈNE
Abstract:
(EN) The invention includes compositions and methods related to erythroid cells comprising exogenous RNA encoding a protein. The exogenous RNA can comprise a heterologous untranslated region comprising a regulatory element. Alternatively or in combination, the exogenous RNA can comprise chemical modifications.
(FR) L'invention comprend des compositions et des procédés associés à des cellules érythroïdes comprenant de l'ARN exogène codant pour une protéine. L'ARN exogène peut comprendre une région non traduite hétérologue comprenant un élément régulateur. En variante ou en combinaison, l'ARN exogène peut comprendre des modifications chimiques.
Designated States: AE, AG, AL, AM, AO, AT, AU, AZ, BA, BB, BG, BH, BN, BR, BW, BY, BZ, CA, CH, CL, CN, CO, CR, CU, CZ, DE, DJ, DK, DM, DO, DZ, EC, EE, EG, ES, FI, GB, GD, GE, GH, GM, GT, HN, HR, HU, ID, IL, IN, IR, IS, JO, JP, KE, KG, KH, KN, KP, KR, KW, KZ, LA, LC, LK, LR, LS, LU, LY, MA, MD, ME, MG, MK, MN, MW, MX, MY, MZ, NA, NG, NI, NO, NZ, OM, PA, PE, PG, PH, PL, PT, QA, RO, RS, RU, RW, SA, SC, SD, SE, SG, SK, SL, SM, ST, SV, SY, TH, TJ, TM, TN, TR, TT, TZ, UA, UG, US, UZ, VC, VN, ZA, ZM, ZW
African Regional Intellectual Property Organization (ARIPO) (BW, GH, GM, KE, LR, LS, MW, MZ, NA, RW, SD, SL, ST, SZ, TZ, UG, ZM, ZW)
Eurasian Patent Office (AM, AZ, BY, KG, KZ, RU, TJ, TM)
European Patent Office (EPO) (AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR)
African Intellectual Property Organization (BF, BJ, CF, CG, CI, CM, GA, GN, GQ, GW, KM, ML, MR, NE, SN, TD, TG)
Publication Language: English (EN)
Filing Language: English (EN)