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1. (WO2018005805) EXON SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY
Latest bibliographic data on file with the International Bureau    Submit observation

Pub. No.:    WO/2018/005805    International Application No.:    PCT/US2017/040017
Publication Date: 04.01.2018 International Filing Date: 29.06.2017
IPC:
C07F 9/6533 (2006.01), C12N 15/113 (2010.01), A61K 31/7088 (2006.01), A61P 21/00 (2006.01)
Applicants: SAREPTA THERAPEUTICS, INC. [US/US]; 215 First Street, Suite 415 Cambridge, MA 02142 (US)
Inventors: FRANK, Diane, Elizabeth; (US).
BESTWICK, Richard, K.; (US)
Agent: MANDRAGOURAS, Amy, E.; (US).
DIGIORGIO, Jeanne, M.; (US).
BRULEY, Kenneth, C.; (US).
CANNING, Kevin, J.; (US).
DUKES, Mark, C.; (US)
Priority Data:
62/357,072 30.06.2016 US
62/356,923 30.06.2016 US
Title (EN) EXON SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY
(FR) SAUTS D'EXONS OLIGOMÈRES POUR LA DYSTROPHIE MUSCULAIRE
Abstract: front page image
(EN)Antisense oligomers complementary to a selected target site in the human dystrophin gene to induce exon 45 skipping are described.
(FR)Des molécules antisens capables de se lier à un site cible sélectionné du gène de la dystrophine humaine pour induire le saut de l'exon 45 sont décrites.
Designated States: AE, AG, AL, AM, AO, AT, AU, AZ, BA, BB, BG, BH, BN, BR, BW, BY, BZ, CA, CH, CL, CN, CO, CR, CU, CZ, DE, DJ, DK, DM, DO, DZ, EC, EE, EG, ES, FI, GB, GD, GE, GH, GM, GT, HN, HR, HU, ID, IL, IN, IR, IS, JO, JP, KE, KG, KH, KN, KP, KR, KW, KZ, LA, LC, LK, LR, LS, LU, LY, MA, MD, ME, MG, MK, MN, MW, MX, MY, MZ, NA, NG, NI, NO, NZ, OM, PA, PE, PG, PH, PL, PT, QA, RO, RS, RU, RW, SA, SC, SD, SE, SG, SK, SL, SM, ST, SV, SY, TH, TJ, TM, TN, TR, TT, TZ, UA, UG, US, UZ, VC, VN, ZA, ZM, ZW.
African Regional Intellectual Property Organization (BW, GH, GM, KE, LR, LS, MW, MZ, NA, RW, SD, SL, ST, SZ, TZ, UG, ZM, ZW)
Eurasian Patent Organization (AM, AZ, BY, KG, KZ, RU, TJ, TM)
European Patent Office (AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR)
African Intellectual Property Organization (BF, BJ, CF, CG, CI, CM, GA, GN, GQ, GW, KM, ML, MR, NE, SN, TD, TG).
Publication Language: English (EN)
Filing Language: English (EN)