WIPO logo
Mobile | Deutsch | Español | Français | 日本語 | 한국어 | Português | Русский | 中文 | العربية |
PATENTSCOPE

Search International and National Patent Collections
World Intellectual Property Organization
Search
 
Browse
 
Translate
 
Options
 
News
 
Login
 
Help
 
Machine translation
1. (WO2014186579) ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE CENTRAL NERVOUS SYSTEM
Latest bibliographic data on file with the International Bureau   

Pub. No.:    WO/2014/186579    International Application No.:    PCT/US2014/038209
Publication Date: 20.11.2014 International Filing Date: 15.05.2014
IPC:
A01N 63/00 (2006.01), C12N 15/00 (2006.01), C12N 15/86 (2006.01)
Applicants: REGENTS OF THE UNIVERSITY OF MINNESOTA [US/US]; Suite 600 McNamara Alumni Ctr. 200 Oak Street SE Minneapolis, Minnesota 55455 (US).
REGENXBIO Inc. [US/US]; (US)
Inventors: McIvor, R., Scott; (US).
BELUR, Lalitha R.; (US).
LOW, Walter; (US).
FAIRBANKS, Carolyn; (US).
KOZARSKY, Karen; (US)
Agent: PERDOK, Monique M.,; Schwegman, Lundberg & Woessner, P.A. P.O. Box 2938 Minneapolis, Minnesota 55402 (US)
Priority Data:
61/823,757 15.05.2013 US
Title (EN) ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE CENTRAL NERVOUS SYSTEM
(FR) TRANSFERT GÉNIQUE AU SYSTÈME NERVEUX CENTRAL À MÉDIATION PAR UN VIRUS ADÉNO-ASSOCIÉ
Abstract: front page image
(EN)A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease.
(FR)L'invention concerne une méthode pour prévenir, inhiber ou traiter un ou plusieurs symptômes associés à une maladie du système nerveux central par administration intra-thécale, intra-cérébro-ventriculaire ou endovasculaire d'un rAAV codant pour un produit génique associé à la maladie, par exemple, à un mammifère dans lequel le produit génique est absent ou présent à un taux réduit par rapport à un mammifère sans la maladie.
Designated States: AE, AG, AL, AM, AO, AT, AU, AZ, BA, BB, BG, BH, BN, BR, BW, BY, BZ, CA, CH, CL, CN, CO, CR, CU, CZ, DE, DK, DM, DO, DZ, EC, EE, EG, ES, FI, GB, GD, GE, GH, GM, GT, HN, HR, HU, ID, IL, IN, IR, IS, JP, KE, KG, KN, KP, KR, KZ, LA, LC, LK, LR, LS, LT, LU, LY, MA, MD, ME, MG, MK, MN, MW, MX, MY, MZ, NA, NG, NI, NO, NZ, OM, PA, PE, PG, PH, PL, PT, QA, RO, RS, RU, RW, SA, SC, SD, SE, SG, SK, SL, SM, ST, SV, SY, TH, TJ, TM, TN, TR, TT, TZ, UA, UG, US, UZ, VC, VN, ZA, ZM, ZW.
African Regional Intellectual Property Organization (BW, GH, GM, KE, LR, LS, MW, MZ, NA, RW, SD, SL, SZ, TZ, UG, ZM, ZW)
Eurasian Patent Organization (AM, AZ, BY, KG, KZ, RU, TJ, TM)
European Patent Office (AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR)
African Intellectual Property Organization (BF, BJ, CF, CG, CI, CM, GA, GN, GQ, GW, KM, ML, MR, NE, SN, TD, TG).
Publication Language: English (EN)
Filing Language: English (EN)