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1. (WO2013162363) RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders
Latest bibliographic data on file with the International Bureau   

Pub. No.: WO/2013/162363 International Application No.: PCT/NL2013/050306
Publication Date: 31.10.2013 International Filing Date: 23.04.2013
IPC:
C12N 15/113 (2010.01) ,A61K 31/7115 (2006.01) ,A61K 31/712 (2006.01) ,A61K 31/7125 (2006.01) ,A61P 25/00 (2006.01)
Applicants: PROSENSA TECHNOLOGIES B.V.[NL/NL]; J.H. Oortweg 21 NL-2333 CH Leiden, NL
Inventors: DE VISSER, Peter Christian; NL
MULDERS, Susan Allegonda Maria; NL
Agent: PALLARD, Caroline; Nederlandsch Octrooibureau J.W. Frisolaan 13 NL-2517 JS The Hague, NL
Priority Data:
12165139.223.04.2012EP
61/636,91423.04.2012US
Title (EN) RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders
(FR) OLIGONUCLÉOTIDES DE MODULATION D'ARN AYANT DES CARACTÉRISTIQUES PERFECTIONNÉES POUR LE TRAITEMENT DE TROUBLES NEUROMUSCULAIRES
Abstract:
(EN) The current invention provides an improved oligonucleotide and its use for treating, ameliorating, preventing, delaying and/or treating a human cis-element repeat instability associated genetic neuromuscular or neurodegenerative disorder.
(FR) La présente invention concerne un oligonucléotide perfectionné et son utilisation pour traiter, améliorer, prévenir, retarder et/ou traiter un trouble neuromusculaire ou neurodégénératif génétique associé à une instabilité de répétition d'élément cis humain.
Designated States: AE, AG, AL, AM, AO, AT, AU, AZ, BA, BB, BG, BH, BN, BR, BW, BY, BZ, CA, CH, CL, CN, CO, CR, CU, CZ, DE, DK, DM, DO, DZ, EC, EE, EG, ES, FI, GB, GD, GE, GH, GM, GT, HN, HR, HU, ID, IL, IN, IS, JP, KE, KG, KM, KN, KP, KR, KZ, LA, LC, LK, LR, LS, LT, LU, LY, MA, MD, ME, MG, MK, MN, MW, MX, MY, MZ, NA, NG, NI, NO, NZ, OM, PA, PE, PG, PH, PL, PT, QA, RO, RS, RU, RW, SC, SD, SE, SG, SK, SL, SM, ST, SV, SY, TH, TJ, TM, TN, TR, TT, TZ, UA, UG, US, UZ, VC, VN, ZA, ZM, ZW
African Regional Intellectual Property Organization (ARIPO) (BW, GH, GM, KE, LR, LS, MW, MZ, NA, RW, SD, SL, SZ, TZ, UG, ZM, ZW)
Eurasian Patent Office (AM, AZ, BY, KG, KZ, RU, TJ, TM)
European Patent Office (EPO) (AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR)
African Intellectual Property Organization (BF, BJ, CF, CG, CI, CM, GA, GN, GQ, GW, ML, MR, NE, SN, TD, TG)
Publication Language: English (EN)
Filing Language: English (EN)