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1. (WO2013148103) NOVEL COMPOUNDS FOR PREVENTING AND/OR TREATING LYSOSOMAL STORAGE DISORDERS AND/OR DEGENERATIVE DISORDERS OF THE CENTRAL NERVOUS SYSTEM
Latest bibliographic data on file with the International Bureau   

Pub. No.:    WO/2013/148103    International Application No.:    PCT/US2013/029612
Publication Date: 03.10.2013 International Filing Date: 07.03.2013
IPC:
C07D 211/44 (2006.01), A61K 31/445 (2006.01), A61P 25/00 (2006.01)
Applicants: AMICUS THERAPEUTICS, INC. [US/US]; 1 Cedarbrook Drive Cranbury, New Jersey 08512 (US)
Inventors: BOYD, Robert; (US).
RYBCZYNSKI, Philip, J.; (US).
SHETH, Kamlesh; (US)
Agent: ALEGRIA, Rory, P.; Servilla Whitney LLC 33 Wood Avenue South Second Floor, Suite 210 Iselin, New Jersey 08830 (US)
Priority Data:
61/616,159 27.03.2012 US
Title (EN) NOVEL COMPOUNDS FOR PREVENTING AND/OR TREATING LYSOSOMAL STORAGE DISORDERS AND/OR DEGENERATIVE DISORDERS OF THE CENTRAL NERVOUS SYSTEM
(FR) NOUVEAUX COMPOSÉS POUR LA PRÉVENTION ET/OU LE TRAITEMENT DES TROUBLES DE STOCKAGE DES LYSOSOMES ET/OU DES TROUBLES DÉGÉNÉRATIFS DU SYSTÈME NERVEUX CENTRAL
Abstract: front page image
(EN)Described are novel salts of the compound (3R,4R,5S)-5-(difluoromethyl) piperidine-3,4-diol, as well as methods of using the same for preventing and/or treating lysosomal storage disorders and/or degenerative disorders of the central nervous system. In particular, the present invention provides methods for preventing and/or treating Gaucher's disease and/or Parkinson's disease.
(FR)L'invention concerne de nouveaux sels du composé (3R,4R,5S)-5- (difluorométhyl)pipéridine-3,4-diol, ainsi que des méthodes d'utilisation de ceux-ci pour la prévention et/ou le traitement des troubles de stockage des lysosomes et/ou des troubles dégénératifs du système nerveux central. En particulier, la présente invention concerne des méthodes de prévention et/ou traitement de la maladie de Gaucher et/ou de la maladie de Parkinson.
Designated States: AE, AG, AL, AM, AO, AT, AU, AZ, BA, BB, BG, BH, BN, BR, BW, BY, BZ, CA, CH, CL, CN, CO, CR, CU, CZ, DE, DK, DM, DO, DZ, EC, EE, EG, ES, FI, GB, GD, GE, GH, GM, GT, HN, HR, HU, ID, IL, IN, IS, JP, KE, KG, KM, KN, KP, KR, KZ, LA, LC, LK, LR, LS, LT, LU, LY, MA, MD, ME, MG, MK, MN, MW, MX, MY, MZ, NA, NG, NI, NO, NZ, OM, PA, PE, PG, PH, PL, PT, QA, RO, RS, RU, RW, SC, SD, SE, SG, SK, SL, SM, ST, SV, SY, TH, TJ, TM, TN, TR, TT, TZ, UA, UG, US, UZ, VC, VN, ZA, ZM, ZW.
African Regional Intellectual Property Organization (BW, GH, GM, KE, LR, LS, MW, MZ, NA, RW, SD, SL, SZ, TZ, UG, ZM, ZW)
Eurasian Patent Organization (AM, AZ, BY, KG, KZ, RU, TJ, TM)
European Patent Office (AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR)
African Intellectual Property Organization (BF, BJ, CF, CG, CI, CM, GA, GN, GQ, GW, ML, MR, NE, SN, TD, TG).
Publication Language: English (EN)
Filing Language: English (EN)